Lysosomal Storage Disease Mouse Models

Lysosomal storage disorders (LSDs) are rare genetic conditions that cause a buildup of toxic materials in the cells of various organs. As part of our rare disease models platform, WuXi AppTec offers an extensive panel of LSD mouse models, including Gaucher disease, Pompe disease, Fabry disease, and Hurler syndrome (MPS I). Our service platform supports efficacy, toxicity, and PK/PD studies for all of these models.

Learn more about our Rare Disease Platform by clicking here.